Bêta thalassémies
- Nature News (2010)
Gene-therapy hope for β-thalassaemia patients
- Nature (2010)
Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
- Cold Spring Harb Perspect Med. (2012)
Development of Gene Therapy for Thalassemia
- Journal of Blood Medicine (2015)
Recent trends in the gene therapy
- Hum Gene Ther. (2016)
Cell and Gene Therapy for the Beta-Thalassemias: Advances and Prospects
- Biomedical Journal (2016)
Current and future alternative therapies for beta-thalassemia major
- INSERM (2017)
Une double thérapie génique contre la drépanocytose
- Mol Ther. (2017)
Gene Therapy for β-Hemoglobinopathies
- Appl Clin Genet (2019)
Gene Therapy For Beta-Thalassemia: Updated Perspectives
- Frontiers in pharmacology (2021)
- N Engl J Med. (2021)
- Nat Med. (2022)
Long-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies: the HGB-205 trial